Abstracts
Harrop, J.S., Poulsen, D., Maragakis, N., Xiao, W., Liu, Y., Liu, J., Rothstein, J., Freese, A., During, M. (2000): Use of a Gene Therapy Vector (recombinant AAV) to Transduce Neurons and Astrocytes within the Rat Spinal Cord Parenchyma. Annual Meeting of the Congress of Neurological Surgeons, Abstract 279.
Leone, P., Freese, A., Latsko, M., McPhee, S., During, M.J., Janson, C.G. (2001): Comparison of Viral and Non-Viral Vectors for Gene Therapy of Canavan Disease. Proceedings of the European Metabolic Group Meeting, Amsterdam.
Liouterman, L., During, M.J., McPhee, S.W.J., Freese, A., Janson, C.G., Horst, R., Peschle, C., Valtieri, M., Leone, P. (2001): Transplantation of Human Hematopoeitic Stem Cells into Rat Brain: Analysis of Cell Survival and Differentiation. Proceedings 31st Annual Meeting, Society for Neuroscience, Abstract 405.4.
Leone, P., Latsko, M., Haselgrove, J., McPhee, S.W.J., Janson, C.G., Jiao, X.Y., Liouterman, L., Francis, J., Young, D., Lawlor, P.A., Fitzsimons, H., Raniga, S., Bilaniuk, L, Wang, Z., Grant, M., Liu, Y., During, M.J., Freese, A. (2001): Gene Therapy of Canavan Disease using AAV Vectors: A Phase 1 Clinical Trial. Proceedings 31st Annual Meeting, Society for Neuroscience.
Freese, A., Latsko, M., McPhee, S., Janson, C., Bilaniak, L., During, M., Leone, P., (2002): Adenoassociated Virus Vector Gene Transfer into the Human Brain: A Phase1 Trial for Patients with Canavan Disease. Annual Meeting of the American Association of Neurological Surgeons, Abstract 710.
Leone, P., McPhee, S.W.J., Janson, C.G., Liouterman, L., Freese, A. (2002): Brain Gene Transfer using AAV Vectors in the Canavan (Tremor) Rat Model and in Children Affected by Canavan Disease: Targeted Development of Preclinical and Clinical Studies. XIVth International Workshop on Genetic Systems in the Rat (Kyoto, Japan).
Freese, A., Liouterman, Liouterman, L., During, M., McPhee, S., Janson, C., Leone, P. (2002): Transplantation of Human Hematopoeitic Stem Cells into Rat Brain; Analysis of Cell Survival and Differentiation. Annual Meeting of the American Association of Neurological Surgeons, Abstract 1132.
Harrop, J., Poulson, D., Darling, M., Freese, A., Maragakis, N., Rothstein, J. (2002): Recombinant AAV Transduces Neurons and Astrocytes within the Rat Spinal Cord. Annual Meeting of the American Associations of Neurological Surgeons, Abstract 768.
Leone, P., Janson, C.G., Freese, A., Samulski, J., Haselgrove, J. Wang, D.J., Bilaniuk, L. (2002): Terapia Genica Nei Pazienti con Malattia Metabolica: Il Modello della Malattia di Canavan. Milanopediatria 2002 (Milan, Italy).
Ohlfest, J., Demorest, Z., Motooka, Y., Oh, S., Chen, E., Scappaticci, F., Ekker, S., Low, W., Freese, A. (2005): Combinatorial Antiangiogenic Gene Therapy Causes Tumor Regression and Improves Survival in Mice Bearing Intracranial Human Glioblastoma by Nonviral Gene transfer Using the Sleeping Beauty Transposon, American Society for Gene Therapy, accepted for a platform presentation.
Freese, A., Ohlfest, J.R., Demorest, Z.L., Motooka, Y., Vengco, I., Oh, S., Chen, E., Scappaticci, F.A., Ekker, S.E., Low, W.C., Largaespada, D.A. (2005): Combinatorial Antiangiogenic Gene Therapy by Nonviral Gene Transfer Using the Sleeping Beauty Transposon Causes Tumor Regression and Improves Survival in Mice Bearing Intracranial Human Glioblastoma, Neurosurgical Society of America, Annual Meeting.